History and exam

Other diagnostic factors

common

history of recurrent infection

May indicate underlying cytopenia.

fatigue

May indicate underlying cytopenia.

pallor

May indicate underlying cytopenia.

history of bleeding or easy bruising

May indicate underlying cytopenia.

tachycardia

May indicate underlying cytopenia.

dyspnea

May indicate underlying cytopenia.

Dyspnea due to pulmonary fibrosis may suggest dyskeratosis congenita.[5]

persistent warts

May suggest inherited GATA2-related disorder.

uncommon

hearing loss or deafness

May suggest Fanconi anemia or inherited GATA2-related disorder.

short stature, pigmentation abnormalities, or urogenital abnormalities

May suggest Fanconi anemia.[4]

nail malformations, reticular rash, oral leukoplakia, or epiphora

May suggest dyskeratosis congenita.[5]

osteoporosis

May suggest dyskeratosis congenita.[5]

premature hair loss/graying

May suggest dyskeratosis congenita.[5]

hyperhidrosis

May suggest dyskeratosis congenita.[5]

dysphagia

Dysphagia due to esophageal stricture may suggest dyskeratosis congenita.[5]

extensive dental caries or tooth loss

May suggest dyskeratosis congenita or Shwachman-Diamond syndrome.[5][6]

steatorrhea

Features of exocrine pancreatic insufficiency such as fat malabsorption may suggest Shwachman-Diamond syndrome.[6]

skeletal dysplasia

May suggest Shwachman-Diamond syndrome.[6]

monocytopenia

May suggest inherited GATA2-related disorder.

nontuberculous mycobacterial infections

May suggest inherited GATA2-related disorder.

pulmonary alveolar proteinosis

May suggest inherited GATA2-related disorder.

congenital lymphedema, Emberger syndrome

May suggest inherited GATA2-related disorder.

immunodeficiency (DCML [dendritic cell, monocyte, B cell, and NK cell deficiency])

May suggest inherited GATA2-related disorder.

Risk factors

strong

drug or toxin exposure

Drugs (e.g., chloramphenicol and non-steroidal anti-inflammatory drugs) and toxins (e.g., chemicals or pesticides) have been implicated in the etiology of AA. However, in only very few instances is there reasonable evidence for an association (from case control studies), and even then it is nearly impossible to prove causality.

The lag time between exposure and disease presentation is usually several weeks to months.[2]

Other drugs with a weak association to AA, which may be coincidental, include penicillamine, gold therapy, and exposures to benzene and dipyrone.[2][3]

paroxysmal nocturnal hemoglobinuria (PNH)

PNH is a rare acquired disorder of the blood characterized by intravascular hemolysis and thrombophilia due to the absence of glycosylphosphatidylinositol-anchored proteins on the membrane surface of blood cells.

PNH and AA are closely related. Patients with PNH can develop AA, and patients with AA often harbor PNH clones even if they do not have the clinical manifestations of PNH. One hypothesis for this relationship is that PNH cells somehow escape the autoimmune attack seen in AA and thus can grow out of proportion to non-PNH cells.[19] See Paroxysmal nocturnal hemoglobinuria.

recent hepatitis

In 5% to 10% of cases, AA can occur in patients with a recent clinical episode of hepatitis.[10] The agent causing hepatitis in these cases is believed to be viral, although it is not any of the known hepatitis virus A-E subtypes.

weak

pregnancy

This association, although described, is poorly understood.[28]

autoimmune disease

Anecdotal reports exist for an association between AA and systemic lupus erythematosus, thymoma, eosinophilic fasciitis, and celiac disease.[29] The mechanism underlying this association is unclear.

family history

Family history of AA or AA-related abnormalities may suggest congenital AA. Increased incidence of cancer among family members may also suggest congenital AA.

Use of this content is subject to our disclaimer