HCL is an indolent mature B-cell neoplasm.[22]Bohn JP, Salcher S, Pircher A, et al. The biology of classic hairy cell leukemia. Int J Mol Sci. 2021 Jul 21;22(15):7780.
https://www.doi.org/10.3390/ijms22157780
http://www.ncbi.nlm.nih.gov/pubmed/34360545?tool=bestpractice.com
Leukemic (hairy) cells typically infiltrate the bone marrow, peripheral blood, spleen, and other hematopoietic organs.[22]Bohn JP, Salcher S, Pircher A, et al. The biology of classic hairy cell leukemia. Int J Mol Sci. 2021 Jul 21;22(15):7780.
https://www.doi.org/10.3390/ijms22157780
http://www.ncbi.nlm.nih.gov/pubmed/34360545?tool=bestpractice.com
Accumulation of hairy cells in the bone marrow, combined with dysregulated cytokine production and reticulin fibrosis, can lead to bone marrow failure and subsequent pancytopenia.[23]Cawley JC. The pathophysiology of the hairy cell. Hematol Oncol Clin North Am. 2006 Oct;20(5):1011-21.
http://www.ncbi.nlm.nih.gov/pubmed/16990104?tool=bestpractice.com
[24]Burthem J, Cawley JC. The bone marrow fibrosis of hairy-cell leukemia is caused by the synthesis and assembly of a fibronectin matrix by the hairy cells. Blood. 1994 Jan 15;83(2):497-504.
http://bloodjournal.hematologylibrary.org/cgi/reprint/83/2/497
http://www.ncbi.nlm.nih.gov/pubmed/8286747?tool=bestpractice.com
Hairy cells infiltrating the spleen can lead to splenomegaly and subsequent sequestration, marginalization, and destruction of healthy blood cells, which contributes to pancytopenia.
Genetic factors
The BRAF V600E mutation is a somatic mutation present in almost all patients with classic HCL.[25]Tiacci E, Trifonov V, Schiavoni G, et al. BRAF mutations in hairy-cell leukemia. N Engl J Med. 2011 Jun 16;364(24):2305-15.
http://www.nejm.org/doi/full/10.1056/NEJMoa1014209#t=article
http://www.ncbi.nlm.nih.gov/pubmed/21663470?tool=bestpractice.com
[26]Tiacci E, Pettirossi V, Schiavoni G, et al. Genomics of hairy cell leukemia. J Clin Oncol. 2017 Mar 20;35(9):1002-10.
https://www.doi.org/10.1200/JCO.2016.71.1556
http://www.ncbi.nlm.nih.gov/pubmed/28297625?tool=bestpractice.com
[27]Troussard X, Maître E, Paillassa J. Hairy cell leukemia 2024: update on diagnosis, risk-stratification, and treatment - annual updates in hematological malignancies. Am J Hematol. 2024 Apr;99(4):679-96.
https://onlinelibrary.wiley.com/doi/10.1002/ajh.27240
http://www.ncbi.nlm.nih.gov/pubmed/38440808?tool=bestpractice.com
The BRAF V600E mutation is an early disease-defining genetic event in classic HCL, and is thought to play a key role in its pathogenesis via activation of the MEK-ERK signaling pathway.[25]Tiacci E, Trifonov V, Schiavoni G, et al. BRAF mutations in hairy-cell leukemia. N Engl J Med. 2011 Jun 16;364(24):2305-15.
http://www.nejm.org/doi/full/10.1056/NEJMoa1014209#t=article
http://www.ncbi.nlm.nih.gov/pubmed/21663470?tool=bestpractice.com
[26]Tiacci E, Pettirossi V, Schiavoni G, et al. Genomics of hairy cell leukemia. J Clin Oncol. 2017 Mar 20;35(9):1002-10.
https://www.doi.org/10.1200/JCO.2016.71.1556
http://www.ncbi.nlm.nih.gov/pubmed/28297625?tool=bestpractice.com
[28]Oscier D, Stamatopoulos K, Mirandari A, et al. The genomics of hairy cell leukaemia and splenic diffuse red pulp lymphoma. Cancers (Basel). 2022 Jan 29;14(3):697.
https://www.doi.org/10.3390/cancers14030697
http://www.ncbi.nlm.nih.gov/pubmed/35158965?tool=bestpractice.com
Constitutive activity of this pathway is thought to lead to increased cell proliferation, survival, and ultimately malignancy.[25]Tiacci E, Trifonov V, Schiavoni G, et al. BRAF mutations in hairy-cell leukemia. N Engl J Med. 2011 Jun 16;364(24):2305-15.
http://www.nejm.org/doi/full/10.1056/NEJMoa1014209#t=article
http://www.ncbi.nlm.nih.gov/pubmed/21663470?tool=bestpractice.com
[26]Tiacci E, Pettirossi V, Schiavoni G, et al. Genomics of hairy cell leukemia. J Clin Oncol. 2017 Mar 20;35(9):1002-10.
https://www.doi.org/10.1200/JCO.2016.71.1556
http://www.ncbi.nlm.nih.gov/pubmed/28297625?tool=bestpractice.com
[29]Ahmadzadeh A, Shahrabi S, Jaseb K, et al. BRAF Mutation in Hairy Cell Leukemia. Oncol Rev. 2014 Sep 23;8(2):253.
https://www.doi.org/10.4081/oncol.2014.253
http://www.ncbi.nlm.nih.gov/pubmed/25992240?tool=bestpractice.com
The BRAF V600E mutation is absent in HCL variant (HCL-V), a separate disease entity (also known as splenic B-cell lymphoma/leukemia with prominent nucleoli [SBLPN]) that is more aggressive than HCL.[1]Alaggio R, Amador C, Anagnostopoulos I, et al. The 5th edition of the World Health Organization classification of haematolymphoid tumours: lymphoid neoplasms. Leukemia. 2022 Jul;36(7):1720-48.
https://www.doi.org/10.1038/s41375-022-01620-2
http://www.ncbi.nlm.nih.gov/pubmed/35732829?tool=bestpractice.com
Other chromosomal and genetic abnormalities reported in HCL include trisomy 5, trisomy 12, chromosome 5q13 deletion, and p53 mutation.[30]Forconi F, Sahota SS, Raspadori D, et al. Hairy cell leukemia: at the crossroad of somatic mutation and isotype switch. Blood. 2004 Nov 15;104(10):3312-7.
http://bloodjournal.hematologylibrary.org/cgi/content/full/104/10/3312
http://www.ncbi.nlm.nih.gov/pubmed/15284115?tool=bestpractice.com
[31]Konig EA, Kusser WC, Day C, et al. p53 mutations in hairy cell leukemia. Leukemia. 2000 Apr;14(4):706-11.
http://www.ncbi.nlm.nih.gov/pubmed/10764158?tool=bestpractice.com
[32]Zuzel M, Cawley JC. The biology of hairy cells. Best Pract Res Clin Haematol. 2003 Mar;16(1):1-13.
http://www.ncbi.nlm.nih.gov/pubmed/12670461?tool=bestpractice.com