History and exam

Key diagnostic factors

common

history of pituitary/hypothalamic disease

Strong risk factors for AVP-D include pituitary surgery, craniopharyngioma, pituitary stalk lesions, traumatic head injury, and congenital pituitary malformations.[1]​​[3][15][38]

family history/genetic mutations

AVP-R may occur in patients with loss-of-function mutations in the AVP receptor pathway, which are inherited in an X-linked or autosomal-recessive pattern.[5][10][43]​ AVP-D may occur in patients with Wolfram syndrome and AVP-neurophysin gene mutations, inherited in an autosomal-dominant pattern.[37][39]​​

history of lithium therapy (or certain other drugs)

AVP-R occurs in up to 40% of patients receiving long-term lithium therapy.[9] Other drugs associated with AVP-R may include demeclocycline, cisplatin, colchicine, gentamicin, rifampicin, and sevoflurane.[5][42]

history of autoimmune disorders

AVP-D is associated with other endocrine autoimmune disorders. In one study, 26% of patients with AVP-D had an associated autoimmune disorder - most frequently Hashimoto's thyroiditis (16.7%) and diabetes mellitus type 1 (5.3%).[29]

polyuria

Volumes ranging from 3 litres to >20 litres per day (or >50 mL/kg/24h).[53]​ This must be distinguished from non-polyuric urinary frequency.​[3]

increased thirst/polydipsia

Fluid intake increases to match renal water loss, leading to significant polydipsia.

Other diagnostic factors

common

nocturia

Significant nocturia is a common presenting feature.[10] Children may have bedwetting.[26]

uncommon

signs of volume depletion

If thirst is decreased (e.g., due to primary pathology, reduced consciousness) or access to free water is limited (e.g., non-availability, disability, intercurrent illness), the patient may become dehydrated and develop hypernatraemia.​[54]

Signs include dry mucous membranes, poor skin turgor, tachycardia, hypotension, and, in severe cases, shock.

non-specific central nervous system symptoms of hypernatraemia

If thirst is decreased (e.g., due to primary pathology, reduced consciousness) or access to free water is limited (e.g., non-availability, disability, intercurrent illness), the patient may become dehydrated and develop hypernatraemia.​[54]

Symptoms and signs of hypernatraemia are non-specific. They include irritability, restlessness, lethargy, spasticity, and hyper-reflexia. If severe, delirium, seizures, and coma may be present.[55]

visual field defects

May indicate a previous or existing pituitary mass.[3]

endocrine signs

In patients with previous functional pituitary macro-adenoma, there may be clinical signs of acromegaly or Cushing's syndrome (if not in remission). Postsurgical AVP-D may be associated with clinical hypopituitarism.

focal motor deficits

May be present due to previous or co-presenting intracranial pathology such as tumour, head injury, hydrocephalus, meningitis, or encephalitis.

sensorineural deafness and visual failure

May reflect additional components of Wolfram syndrome, a progressive neurodegenerative disorder characterised by diabetes mellitus and optic atrophy, with varying frequency of AVP-D and sensorineural deafness.[39]

skin lesions

Presence of papular rashes or ulcers may suggest systemic Langerhans' cell histiocytosis, which can cause AVP-D.

Similarly, the presence of erythema nodosum may suggest sarcoidosis as a cause of AVP-D or AVP-R.

Risk factors

strong

pituitary surgery

Pituitary or para-pituitary surgery is a common cause of AVP-D.[49]​ It is uncommon for AVP-D to present preoperatively in patients with pituitary adenomatous disease. Preoperative (or at time of presentation) AVP-D are reported in craniopharyngioma, infiltrative hypothalamic/pituitary stalk lesions, or pituitary metastases.[3] AVP-D after pituitary surgery may be transient or permanent. Rarely after pituitary surgery, there may be a classical triple-phase response: an acute initial AVP-D, followed by a transient antidiuretic phase (syndrome of inappropriate antidiuresis), subsequently progressing to permanent AVP-D.[12]

craniopharyngioma

In contrast to most intracranial tumours, AVP-D is common at presentation in patients with craniopharyngioma (8% to 35%). Incidence increases postoperatively (70% to 90%).[13]

There may also be associated thirst abnormalities, either as a consequence of more extensive hypothalamic involvement of the tumour or as a consequence of intervention.[14]

pituitary stalk lesions

Lesions involving the pituitary stalk are recognised causes of AVP-D.​[4][25]

Pituitary stalk involvement is common in Langerhans' cell histiocytosis. One study reported stalk involvement in 71% of patients at diagnosis, and persisting in 24% of patients after 5 years.[50] AVP-D is a well-recognised complication, occurring in up to 24% of patients.[18] Other conditions leading to pituitary stalk involvement and AVP-D include germinoma, intracranial metastases, granulomatous disease (e.g., sarcoidosis and tuberculosis), and lymphocytic infundibulohypophysitis.​[1]

traumatic brain injury

AVP-D is common following traumatic brain injury.[15] It is most frequently transient, developing in 21% to 26% of cases.[16][17]​ Permanent AVP-D has been reported in approximately 7% of cases.[16]

congenital pituitary abnormalities

Congenital malformations involving the pituitary or hypothalamus may be associated with AVP-D.​[38]

use of certain drugs

AVP-R occurs in up to 40% of patients receiving long-term lithium therapy, but the incidence of this adverse effect has been reported to be as high as 85%.[9][10]​ Other drugs associated with AVP-R may include demeclocycline, cisplatin, colchicine, gentamicin, rifampicin, and sevoflurane.[5][42]

AVP-D is less commonly caused by drugs. It has been reported in association with phenytoin.[33]

hypophysitis

AVP-D is associated with hypophysitis either in isolation or in combination with anterior pituitary hormone dysfunction.[51]

autoimmune disease

AVP-D is associated with other autoimmune endocrine disorders - most frequently Hashimoto's thyroiditis (16.7%) and diabetes mellitus type 1 (5.3%).[29]

Autoantibodies to arginine vasopressin-secreting cells (AVPcAb) have been reported in 33% of patients with idiopathic (non-structural) AVP-D.[29]

family history/genetic mutations

There are familial (inherited) forms of both AVP-D and AVP-R. AVP-R may occur in patients with loss-of-function mutations in the AVP receptor pathway.[5][10]​​ Most common are mutations in the AVPR2 receptor, inherited in an X-linked recessive pattern. Aquaporin-2 water channel gene mutations (autosomal recessive) and urea transporter-B mutations also produce AVP-R.[5][10]​​[37]​​

Familial AVP-D accounts for approximately 1% to 5% of all cases of AVP-D. It is usually an autosomal dominantly inherited condition due to a mutation in the AVP-NPII gene located on chromosome 20p135. This condition often has many family members presenting with clinical AVP-D early on in life.[37]​ AVP-D may also occur as a component of Wolfram syndrome, an autosomal recessive, progressive neurodegenerative disorder characterised by diabetes mellitus and optic atrophy, with varying frequency of AVP-D and sensorineural deafness.[39] 

weak

pregnancy

Pregnancy is associated with a number of changes in salt and water regulation.[44] There is a fourfold increase in metabolic clearance of AVP in pregnancy, due to placental production of vasopressinase/oxytocinase. This can un-mask previously partial AVP-D.​[6][45]​ Transient gestational AVP-D has been reported in patients with pre-eclampsia, HELLP (haemolysis, elevated liver enzymes, and low platelet count) syndrome and acute fatty liver disease due to impaired hepatic degradation of vasopressinase.

subarachnoid haemorrhage

AVP-D may develop following subarachnoid haemorrhage involving the anterior communicating artery supplying the anterior hypothalamus.[32]

renal sarcoidosis

Recognised cause of AVP-R.[21]

renal amyloidosis

Recognised cause of AVP-R.[5]

hypercalcaemia or hypokalaemia

Recognised cause of AVP-R.[5]

release of obstructive uropathy

Recognised cause of AVP-R.[5][10]

previous central nervous system infections

AVP-D may develop as a late complication of meningitis or encephalitis.[22][23][30][31]

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