History and exam

Key diagnostic factors

common

pallor

Common finding on physical examination due to anaemia.

ecchymoses or petechiae

Common finding on physical examination due to thrombocytopenia.

Other diagnostic factors

common

fatigue

Many patients have fatigue. Caused by bone marrow infiltration, anaemia, or the action of associated systemic inflammatory cytokines.

dizziness

Many patients have dizziness. Caused by bone marrow infiltration, anaemia, or the action of associated systemic inflammatory cytokines.

palpitations

Many patients have palpitations. Caused by bone marrow infiltration, anaemia, or the action of associated systemic inflammatory cytokines.

dyspnoea

Many patients have dyspnoea. Caused by bone marrow infiltration, anaemia, pulmonary infection, or the action of associated systemic inflammatory cytokines.

fever and infections

Many patients present with fever and/or other signs and symptoms of infection due to neutropenia.

Notable sites of infection include mouth, teeth (dental abscess), nasopharynx, pulmonary, and perianal.[54][55]

lymphadenopathy

Common finding on physical examination due to extramedullary leukaemic infiltration.

Enlarged lymph nodes are frequently the initial cause for seeking medical attention by the patient.

hepatosplenomegaly

Common finding on physical examination due to extramedullary leukaemic infiltration.

mucosal bleeding

Bleeding from the gums or nose or menorrhagia in females may be due to associated thrombocytopenia.

uncommon

skin and/or testicular mass

May be present due to extramedullary leukaemic infiltration.

skin infiltration

Leukaemia cutis may be present.

The presence of cutaneous ulcers (e.g., Sweet's syndrome or pyoderma gangrenosum) may indicate underlying malignancy.

Sweet's syndrome is characterised by fever, leukocytosis (symptomatic hyperleukocytosis; symptoms include respiratory distress and altered mental status), and tender, erythematous, well-demarcated papules and plaques on skin, which show dense neutrophilic infiltrates.

Pyoderma gangrenosum is characterised by presence of ulcers on leg, or less commonly the hands. Develops as a consequence of immune dysfunction and may be associated with AML.

gingival enlargement

Consequence of leukaemic infiltration; gingivae bleed easily due to associated thrombocytopenia.

bone pain

Related to bone marrow infiltration by blast cells.

skin chloromas

May be present due to extramedullary leukaemic infiltration.

abdominal pain

Severe abdominal pain may be present due to leukaemic infiltration or infection.

Acute abdomen is rarely noted on physical examination.

neurological symptoms (e.g., headache, confusion)

May be present due to meningeal leukaemic infiltration.

Risk factors

strong

age over 65 years

AML is more common in older adults.[5][6]​​​​ In the US, approximately 61% of cases are diagnosed in people aged 65 years or over (2017-2021 data).[5] The median age at diagnosis is 69 years in the US.[5]

In the UK, approximately 66% of cases are diagnosed in people aged 65 years or over (2017 to 2018 data).[6]

previous treatment with chemotherapy

Alkylating agents (e.g., cyclophosphamide, melphalan, mechlorethamine) predispose to AML (latency of 5-10 years), with associated chromosome 5 and 7 abnormalities.[7][8][11]​​​​​

Topoisomerase II inhibitors (e.g., etoposide, teniposide, and anthracyclines such as doxorubicin) predispose to AML (latency of 1-5 years), with associated chromosome 11q23 (KMT2A gene) abnormalities.[7][8][11]​​​​​​[12]​ Other cytogenetic abnormalities associated with these agents include t(15;17)(q22;q12), which results in acute promyelocytic leukaemia (APL, a subtype of AML), and t(8;21).

previous haematological disorders

The incidence of AML is increased in patients with previous haematological disorders, including: aplastic anaemia (particularly in the presence of monosomy 7); paroxysmal nocturnal haemoglobinuria; myelodysplastic syndrome (which evolves to AML in approximately 30% of patients); chronic myeloid leukaemia (may progress to myeloid blast crisis); chronic myelomonocytic leukaemia; and myeloproliferative neoplasms (polycythaemia vera, essential thrombocythaemia, primary myelofibrosis).[13][14][15][16][17]

inherited genetic conditions

Inherited chromosomal fragility disorders and bone marrow failure syndromes are associated with an increased risk for AML.[18][19][20]

These include Bloom's syndrome, Wiskott-Aldrich syndrome, ataxia telangiectasia, Kostmann's syndrome, Fanconi's anaemia, dyskeratosis congenita, Shwachman-Diamond syndrome, severe congenital neutropenia, and Diamond-Blackfan anaemia.[1][2]​​[18][19][20][21][22][23][24]

Familial AML may be due to germline mutations of the tumour suppressor gene TP53 (Li-Fraumeni syndrome) or deletion at the carboxy terminus of CEBPA, which encodes a granulocytic differentiation factor.[43][44]

Neurofibromatosis due to abnormalities of the tumour suppressor gene NF1 at chromosome 17q11.2 predisposes to AML, usually in the second decade of life.[45]

constitutional chromosomal abnormalities

Down's syndrome (trisomy 21), Klinefelter's syndrome (XXY), and Patau's syndrome (trisomy 13) are associated with increased risk of AML.[25][26]​​[27]

In those with Down's syndrome who develop AML, additional unbalanced chromosomal abnormalities such as dup(1q), del(6q), del(7p), dup(7q), +8, +11, and del(16q) are distinctive and may contribute to the pathogenesis.[28]

radiation exposure

Historically, survivors of the atomic bombing of Hiroshima and Nagasaki had an increased incidence of myelodysplastic syndromes and AML.[9]​ This incidence was highest in those under 20 years of age at the time of exposure.[46]

Radiotherapy, particularly in combination with alkylating agents (e.g., cyclophosphamide, melphalan), also predisposes to AML.[7][8][47]​​

benzene exposure

A 2- to 10-fold increase in leukaemia, predominantly AML, occurs in painters, printers, petroleum refinery workers, and chemical, rubber, and shoe manufacturing workers exposed to benzene.[48]

Additional benzene exposure occurs due to smoking or from unleaded petrol vapours.[49] The risk of leukaemogenesis is proportionate to the level of exposure.[50]

Benzene exposure is associated with a depletion of CD4+ lymphocytes.[51]

weak

environmental exposures

Smoking has been found to be associated with the development of AML.[29]​​[30]

Use of hair dyes and alcohol consumption has also been linked with AML, but the evidence is weak and inconsistent.[31][32][33][34]​​​​​​​

A 1.1- to 1.4-fold increased risk of AML occurs in agricultural workers. This has been attributed to pesticides, diesel fuel, fertilisers, and infectious agents.[35] Abattoir workers, veterinarians, and meat packagers also have an increased risk.[36][37]​​​​

male sex

AML is more common in men, with a male to female ratio of approximately 1.5:1 in the US.[5] In the UK, 56% of AML cases are in males and 44% are in females.[6]

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