S-1 (tegafur, 5-chloro-2,4-dihydropyrimidine, and potassium oxonate)
S-1 (tegafur, 5-chloro-2,4-dihydropyrimidine, and potassium oxonate), a fourth-generation fluoropyrimidine, is prescribed as postoperative adjuvant chemotherapy for stage 2 or 3 gastric cancer in Asia and in some parts of Europe; it is not approved for use in some other countries, including the US.[26]Lordick F, Carneiro F, Cascinu S, et al. Gastric cancer: ESMO clinical practice guideline for diagnosis, treatment and follow-up. Ann Oncol. 2022 Oct;33(10):1005-20.
https://www.annalsofoncology.org/article/S0923-7534(22)01851-8/fulltext
http://www.ncbi.nlm.nih.gov/pubmed/35914639?tool=bestpractice.com
[79]Boku N, Yamamoto S, Fukuda H, et al; Gastrointestinal Oncology Study Group of the Japan Clinical Oncology Group. Fluorouracil versus combination of irinotecan plus cisplatin versus S-1 in metastatic gastric cancer: a randomised phase 3 study. Lancet Oncol. 2009 Nov;10(11):1063-9.
http://www.ncbi.nlm.nih.gov/pubmed/19818685?tool=bestpractice.com
[80]Sasako M, Sakuramoto S, Katai H, et al. Five-year outcomes of a randomized phase III trial comparing adjuvant chemotherapy with S-1 versus surgery alone in stage II or III gastric cancer. J Clin Oncol. 2011 Nov 20;29(33):4387-93.
http://www.ncbi.nlm.nih.gov/pubmed/22010012?tool=bestpractice.com
[81]Yoshida K, Kodera Y, Kochi M, et al. Addition of docetaxel to oral fluoropyrimidine improves efficacy in patients with stage III gastric cancer: interim analysis of JACCRO GC-07, a randomized controlled trial. J Clin Oncol. 2019 May 20;37(15):1296-304.
https://ascopubs.org/doi/10.1200/JCO.18.01138
http://www.ncbi.nlm.nih.gov/pubmed/30925125?tool=bestpractice.com
One Cochrane review reported that, in patients with advanced gastric cancer, S-1 regimens improved overall survival modestly (<1 month) compared with fluorouracil-containing regimens.[57]Wagner AD, Syn NL, Moehler M, et al. Chemotherapy for advanced gastric cancer. Cochrane Database Syst Rev. 2017 Aug 29;(8):CD004064.
https://www.cochranelibrary.com/cdsr/doi/10.1002/14651858.CD004064.pub4/full
http://www.ncbi.nlm.nih.gov/pubmed/28850174?tool=bestpractice.com
Results from a subsequent phase 3 randomised controlled trial suggest that perioperative S-1 plus oxaliplatin (SOX) may have a role in the management of patients with locally advanced gastric cancer undergoing D2 gastrectomy.[82]Zhang X, Liang H, Li Z, et al; RESOLVE study group. Perioperative or postoperative adjuvant oxaliplatin with S-1 versus adjuvant oxaliplatin with capecitabine in patients with locally advanced gastric or gastro-oesophageal junction adenocarcinoma undergoing D2 gastrectomy (RESOLVE): an open-label, superiority and non-inferiority, phase 3 randomised controlled trial. Lancet Oncol. 2021 Aug;22(8):1081-92.
http://www.ncbi.nlm.nih.gov/pubmed/34252374?tool=bestpractice.com
S-1 is used in different doses and schedules in Asian and non-Asian populations.
Bemarituzumab
Bemarituzumab, a first-in-class monoclonal antibody against fibroblast growth factor receptor 2 (FGFR2b), is being investigated as a potential treatment for patients with FGFR2b over-expression and HER2-negative metastatic and locally advanced gastric and gastro-oesophageal adenocarcinoma. Bemarituzmab has been granted breakthrough therapy designation by the US Food and Drug Administration (FDA) in combination with modified FOLFOX6 (fluoropyrimidine, folinic acid, and oxaliplatin) for this patient group, based on an FDA-approved companion diagnostic assay showing at least 10% of tumour cells over-expressing FGFR2b. The randomised phase 2 FIGHT trial showed that the combination of bemarituzumab plus modified FOLFOX6 resulted in numerically longer median progression-free survival and overall survival compared with modified FOLFOX6 alone.[83]Wainberg ZA, Kang YK, Lee KW, et al. Bemarituzumab as first-line treatment for locally advanced or metastatic gastric/gastroesophageal junction adenocarcinoma: final analysis of the randomized phase 2 FIGHT trial. Gastric Cancer. 2024 May;27(3):558-70.
https://link.springer.com/article/10.1007/s10120-024-01466-w
http://www.ncbi.nlm.nih.gov/pubmed/38308771?tool=bestpractice.com
Phase 3 trials are in progress.[84]ClinicalTrials.gov. Bemarituzumab plus chemotherapy and nivolumab versus chemotherapy and nivolumab for FGFR2b overexpressed untreated advanced gastric and gastroesophageal junction cancer. (FORTITUDE-102). ClinicalTrials.gov Identifier: NCT05111626. Sep 2024 [internet publication].
https://clinicaltrials.gov/study/NCT05111626
[85]ClinicalTrials.gov. Bemarituzumab or placebo plus chemotherapy in gastric cancers with fibroblast growth factor receptor 2b (FGFR2b) overexpression (FORTITUDE-101). ClinicalTrials.gov Identifier: NCT04229004. Jun 2024 [internet publication].
https://clinicaltrials.gov/study/NCT05052801
Cinrebafusp alfa
Cinrebafusp alfa, a fusion protein comprising a 4-1BB-targeting anticalin protein and a HER2-targeting antibody, has been granted orphan drug designation by the FDA for the treatment of HER2-high and HER2-low expressing gastric cancers.
Regorafenib
Regorafenib, an oral multikinase inhibitor, prolonged progression-free survival in one phase 2, randomised placebo-controlled trial of patients with refractory advanced gastric adenocarcinoma.[86]Pavlakis N, Sjoquist KM, Martin AJ, et al. Regorafenib for the treatment of advanced gastric cancer (INTEGRATE): a multinational placebo-controlled phase II trial. J Clin Oncol. 2016 Aug 10;34(23):2728-35.
https://ascopubs.org/doi/10.1200/JCO.2015.65.1901
http://www.ncbi.nlm.nih.gov/pubmed/27325864?tool=bestpractice.com
Post-hoc analysis suggested that regorafenib improves deterioration-free survival without an excessively negative effect on quality of life.[87]Martin AJ, Gibbs E, Sjoquist K, et al. Health-related quality of life associated with regorafenib treatment in refractory advanced gastric adenocarcinoma. Gastric Cancer. 2018 May;21(3):473-80.
https://link.springer.com/article/10.1007/s10120-017-0754-1
http://www.ncbi.nlm.nih.gov/pubmed/28815316?tool=bestpractice.com
INTEGRATE-IIa trial showed improved overall survival in participants treated with regorafenib compared with the placebo-treated group in patients with advanced gastro-oesophageal cancer.[88]ClinicalTrials.gov. A study of regorafenib in refractory advanced gastro-oesophageal cancer (INTEGRATEIIa). NCT02773524. Jan 2022 [internet publication].
https://clinicaltrials.gov/ct2/show/NCT02773524
[89]Lam LL, Pavlakis N, Shitara K, et al. INTEGRATE II: randomised phase III controlled trials of regorafenib containing regimens versus standard of care in refractory Advanced Gastro-Oesophageal Cancer (AGOC): a study by the Australasian Gastro-Intestinal Trials Group (AGITG). BMC Cancer. 2023 Feb 22;23(1):180.
https://bmccancer.biomedcentral.com/articles/10.1186/s12885-023-10642-7
http://www.ncbi.nlm.nih.gov/pubmed/36814222?tool=bestpractice.com
One phase 3 trial (INTEGRATE-IIb) evaluating regorafenib plus nivolumab against standard chemotherapy in patients with refractory advanced gastro-oesophageal cancer is in progress.[89]Lam LL, Pavlakis N, Shitara K, et al. INTEGRATE II: randomised phase III controlled trials of regorafenib containing regimens versus standard of care in refractory Advanced Gastro-Oesophageal Cancer (AGOC): a study by the Australasian Gastro-Intestinal Trials Group (AGITG). BMC Cancer. 2023 Feb 22;23(1):180.
https://bmccancer.biomedcentral.com/articles/10.1186/s12885-023-10642-7
http://www.ncbi.nlm.nih.gov/pubmed/36814222?tool=bestpractice.com
[90]ClinicalTrials.gov. RegoNivo vs standard of care chemotherapy in AGOC (INTEGRATEIIb). ClinicalTrials.gov Identifier: NCT04879368. May 2024 [internet publication].
https://clinicaltrials.gov/study/NCT04879368
Margetuximab
Margetuximab is a monoclonal antibody that targets HER2-expressing tumours. It has been granted orphan drug designation by the FDA for the treatment of patients with gastric cancer. A phase 2/3 open-label trial assessing the effectiveness of margetuximab in combination with a checkpoint inhibitor (with or without chemotherapy), for patients with HER2-positive gastric cancer or gastro-oesophageal junction cancer, is ongoing.[91]Catenacci DV, Rosales M, Chung HC, et al. MAHOGANY: margetuximab combination in HER2+ unresectable/metastatic gastric/gastroesophageal junction adenocarcinoma. Future Oncol. 2021 Apr;17(10):1155-64.
https://www.futuremedicine.com/doi/10.2217/fon-2020-1007
http://www.ncbi.nlm.nih.gov/pubmed/33263418?tool=bestpractice.com
[92]ClinicalTrials.gov. Combination margetuximab, retifanlimab, tebotelimab, and chemotherapy phase 2/3 trial in HER2+ gastric/GEJ Cancer (MAHOGANY). NCT04082364. Apr 2022 [internet publication].
https://clinicaltrials.gov/ct2/show/NCT04082364
Evorpacept
Evorpacept is a CD47 checkpoint inhibitor. It has been granted orphan drug designation by the FDA for the treatment of patients with gastric cancer. In one phase 1 trial, 21.1% of patients with gastric cancer responded to treatment with evorpacept plus trastuzumab.[93]Lakhani NJ, Chow LQM, Gainor JF, et al. Evorpacept alone and in combination with pembrolizumab or trastuzumab in patients with advanced solid tumours (ASPEN-01): a first-in-human, open-label, multicentre, phase 1 dose-escalation and dose-expansion study. Lancet Oncol. 2021 Dec;22(12):1740-51.
http://www.ncbi.nlm.nih.gov/pubmed/34793719?tool=bestpractice.com
A phase 2/3 study is in progress.[94]ClinicalTrials.gov. A study of evorpacept (ALX148) in patients with advanced HER2+ gastric cancer (ASPEN-06). NCT05002127. Apr 2022 [internet publication].
https://clinicaltrials.gov/ct2/show/NCT05002127
TJ-CD4B
TJ-CD4B is a bispecific antibody that binds to CLDN18.2-expressing cancer cells and the co-stimulatory molecule 4-1BB expressed on T cells. It has been granted orphan drug designation by the FDA for the treatment of patients with gastric cancer. A phase 1 trial is in progress.[95]ClinicalTrials.gov. Study of TJ033721 in subjects with advanced or metastatic solid tumors. NCT04900818. Apr 2022 [internet publication].
https://clinicaltrials.gov/ct2/show/NCT04900818