The pathophysiology of KS is poorly understood, with the link between genotype and phenotype only partially explained.[4]Gravholt CH, Chang S, Wallentin M, et al. Klinefelter syndrome: integrating genetics, neuropsychology, and endocrinology. Endocr Rev. 2018 Aug 1;39(4):389-423.
https://www.doi.org/10.1210/er.2017-00212
http://www.ncbi.nlm.nih.gov/pubmed/29438472?tool=bestpractice.com
Both hypogonadism and genetic effects are believed to contribute to the spectrum of clinical features associated with KS.[4]Gravholt CH, Chang S, Wallentin M, et al. Klinefelter syndrome: integrating genetics, neuropsychology, and endocrinology. Endocr Rev. 2018 Aug 1;39(4):389-423.
https://www.doi.org/10.1210/er.2017-00212
http://www.ncbi.nlm.nih.gov/pubmed/29438472?tool=bestpractice.com
The androgen receptor (AR) gene is of interest regarding correlation between genotype and phenotypic variation as it contains a highly polymorphic trinucleotide repeat that is correlated with physiologic androgen effects and may be associated with androgen-dependent features of KS.[3]Zitzmann M, Aksglaede L, Corona G, et al. European Academy of Andrology guidelines on Klinefelter syndrome. Endorsing organization: European Society of Endocrinology. Andrology. 2021 Jan;9(1):145-67.
https://www.doi.org/10.1111/andr.12909
http://www.ncbi.nlm.nih.gov/pubmed/32959490?tool=bestpractice.com
Emerging evidence shows that the extra X chromosome leads to profound changes in methylation of DNA and transcriptomic changes, not only on the sex chromosomes but also on all the autosomes, with the phenotypic traits seen in KS explained by organ-specific genomic changes involving multiple genes.[5]Gravholt CH, Ferlin A, Gromoll J, et al. New developments and future trajectories in supernumerary sex chromosome abnormalities: a summary of the 2022 3rd International Workshop on Klinefelter Syndrome, Trisomy X, and XYY. Endocr Connect. 2023 Mar 1;12(3):e220500.
https://www.doi.org/10.1530/EC-22-0500
http://www.ncbi.nlm.nih.gov/pubmed/36598290?tool=bestpractice.com
[11]Viuff M, Skakkebæk A, Johannsen EB, et al. X chromosome dosage and the genetic impact across human tissues. Genome Med. 2023 Mar 28;15(1):21.
https://www.doi.org/10.1186/s13073-023-01169-4
http://www.ncbi.nlm.nih.gov/pubmed/36978128?tool=bestpractice.com
Testicular degeneration and abnormal testicular function begins in childhood (perhaps even in utero) and accelerates during puberty. From early- to mid-puberty onward, impairment of Leydig cells (the primary source of testosterone) results in hypergonadotropic hypogonadism, with extensive fibrosis and hyalinization of seminiferous tubules.[1]Groth KA, Skakkebæk A, Høst C, et al. Clinical review: Klinefelter syndrome - a clinical update. J Clin Endocrinol Metab. 2013 Jan;98(1):20-30.
https://www.doi.org/10.1210/jc.2012-2382
http://www.ncbi.nlm.nih.gov/pubmed/23118429?tool=bestpractice.com
[2]Butler G, Srirangalingam U, Faithfull J, et al. Klinefelter syndrome: going beyond the diagnosis. Arch Dis Child. 2023 Mar;108(3):166-71.
http://www.ncbi.nlm.nih.gov/pubmed/35948402?tool=bestpractice.com
[3]Zitzmann M, Aksglaede L, Corona G, et al. European Academy of Andrology guidelines on Klinefelter syndrome. Endorsing organization: European Society of Endocrinology. Andrology. 2021 Jan;9(1):145-67.
https://www.doi.org/10.1111/andr.12909
http://www.ncbi.nlm.nih.gov/pubmed/32959490?tool=bestpractice.com
[4]Gravholt CH, Chang S, Wallentin M, et al. Klinefelter syndrome: integrating genetics, neuropsychology, and endocrinology. Endocr Rev. 2018 Aug 1;39(4):389-423.
https://www.doi.org/10.1210/er.2017-00212
http://www.ncbi.nlm.nih.gov/pubmed/29438472?tool=bestpractice.com
Most adolescents and adults with KS have azoospermia in the ejaculate. However, pockets of normal spermatic tubular structure and focal spermatogenesis may be found within the highly disordered testicular architecture, perhaps due to a mechanism to eject the supernumerary X chromosome.[1]Groth KA, Skakkebæk A, Høst C, et al. Clinical review: Klinefelter syndrome - a clinical update. J Clin Endocrinol Metab. 2013 Jan;98(1):20-30.
https://www.doi.org/10.1210/jc.2012-2382
http://www.ncbi.nlm.nih.gov/pubmed/23118429?tool=bestpractice.com
[2]Butler G, Srirangalingam U, Faithfull J, et al. Klinefelter syndrome: going beyond the diagnosis. Arch Dis Child. 2023 Mar;108(3):166-71.
http://www.ncbi.nlm.nih.gov/pubmed/35948402?tool=bestpractice.com
[4]Gravholt CH, Chang S, Wallentin M, et al. Klinefelter syndrome: integrating genetics, neuropsychology, and endocrinology. Endocr Rev. 2018 Aug 1;39(4):389-423.
https://www.doi.org/10.1210/er.2017-00212
http://www.ncbi.nlm.nih.gov/pubmed/29438472?tool=bestpractice.com
The additional copy of the SHOX gene in the pseudoautosomal region of the X chromosome may contribute to faster childhood growth but the growth acceleration mechanism is not through increased growth hormone secretion and is therefore presumed to be through a direct genetic effect of the gene on the growth plate.[2]Butler G, Srirangalingam U, Faithfull J, et al. Klinefelter syndrome: going beyond the diagnosis. Arch Dis Child. 2023 Mar;108(3):166-71.
http://www.ncbi.nlm.nih.gov/pubmed/35948402?tool=bestpractice.com
The effect of an additional X chromosome on brain function and cognitive development has been well studied but the mechanisms of the chromosomal interference and any explanations for the nonspecific effects seen in KS are poorly understood.[12]van Rijn S, Swaab H, Aleman A, et al. X chromosomal effects on social cognitive processing and emotion regulation: a study with Klinefelter men (47,XXY). Schizophr Res. 2006 Jun;84(2-3):194-203.
http://www.ncbi.nlm.nih.gov/pubmed/16603340?tool=bestpractice.com
[13]van Rijn S. A review of neurocognitive functioning and risk for psychopathology in sex chromosome trisomy (47,XXY, 47,XXX, 47, XYY). Curr Opin Psychiatry. 2019 Mar;32(2):79-84.
https://www.doi.org/10.1097/YCO.0000000000000471
http://www.ncbi.nlm.nih.gov/pubmed/30689602?tool=bestpractice.com