Patients with severe haematological or neurological symptoms of vitamin B12 deficiency require immediate treatment with an intensive regimen of cyanocobalamin or hydroxocobalamin over 1 month, followed by ongoing maintenance doses.
Patients with mild to moderate symptoms of vitamin B12 deficiency should be started and continue on maintenance-level doses of cyanocobalamin or hydroxocobalamin.
Asymptomatic patients with a high risk of vitamin B12 deficiency (e.g., vegans and strict vegetarians, older patients, those with chronic gastrointestinal [GI] illnesses) require maintenance-level doses of cyanocobalamin or hydroxocobalamin (because haematological and neurological complications of vitamin B12 deficiency may be irreversible once they develop).
If the cause of the vitamin B12 deficiency is not yet established, or if vitamin B12 deficiency is clinically suspected despite normal or high serum vitamin B12 levels, treatment should be commenced while awaiting results of further investigations (e.g., anti-intrinsic factor antibody testing).
Vitamin B12 therapy options
Options available include parenteral (intramuscular or subcutaneous), oral, sublingual, or intranasal cyanocobalamin.
Parenteral cyanocobalamin or hydroxocobalamin
By far the most reliable and most familiar treatment for vitamin B12 deficiency, particularly for patients with severe anaemia and/or neurological disease (sub-acute combined spinal degeneration, dementia, or cognitive impairment).[42]Stabler SP. Clinical practice. Vitamin B12 deficiency. N Engl J Med. 2013 Jan 10;368(2):149-60.
http://www.ncbi.nlm.nih.gov/pubmed/23301732?tool=bestpractice.com
In Europe, parenteral hydroxocobalamin is more commonly used than parenteral cyanocobalamin. Hydroxocobalamin is retained longer in the body than cyanocobalamin, but superiority to cyanocobalamin has not been established in clinical trials.
Oral cyanocobalamin
Preferred to intramuscular administration.[82]Sanz-Cuesta T, Escortell-Mayor E, Cura-Gonzalez I, et al. Oral versus intramuscular administration of vitamin B12 for vitamin B12 deficiency in primary care: a pragmatic, randomised, non-inferiority clinical trial (OB12). BMJ Open. 2020 Aug 20;10(8):e033687.
https://www.doi.org/10.1136/bmjopen-2019-033687
http://www.ncbi.nlm.nih.gov/pubmed/32819927?tool=bestpractice.com
High-dose oral cyanocobalamin can be adequately absorbed, even in patients with pernicious anaemia or significant terminal ileum resection.[83]Kuzminski AM, Del Giacco EJ, Allen RH, et al. Effective treatment of cobalamin deficiency with oral cobalamin. Blood. 1998 Aug 15;92(4):1191-8.
http://www.bloodjournal.org/content/92/4/1191.long
http://www.ncbi.nlm.nih.gov/pubmed/9694707?tool=bestpractice.com
[84]Berlin H, Berlin R, Brante G. Oral treatment of pernicious anemia with high doses of vitamin B12 without intrinsic factor. Acta Med Scand. 1968 Oct;184(4):247-58.
http://www.ncbi.nlm.nih.gov/pubmed/5751528?tool=bestpractice.com
[85]Gomollón F, Gargallo CJ, Muñoz JF, et al. Oral cyanocobalamin is effective in the treatment of vitamin B12 deficiency in Crohn's disease. Nutrients. 2017 Mar 20;9(3):E308.
https://www.mdpi.com/2072-6643/9/3/308/htm
http://www.ncbi.nlm.nih.gov/pubmed/28335526?tool=bestpractice.com
Absorption can be maximised by administering on an empty stomach. Findings from one Cochrane review suggest that oral cyanocobalamin is at least as effective as intramuscular cyanocobalamin in patients with vitamin B12 deficiency.[86]Wang H, Li L, Qin LL, et al. Oral vitamin B12 versus intramuscular vitamin B12 for vitamin B12 deficiency. Cochrane Database Syst Rev. 2018 Mar 15;(3):CD004655.
http://cochranelibrary-wiley.com/doi/10.1002/14651858.CD004655.pub3/full
http://www.ncbi.nlm.nih.gov/pubmed/29543316?tool=bestpractice.com
Sublingual and intranasal cyanocobalamin
Although effective, sublingual and intranasal cyanocobalamin are generally not used in the treatment of vitamin B12 deficiency due to limited evidence and limited knowledge regarding optimal dosing.[87]Sharabi A, Cohen E, Sulkes J, et al. Replacement therapy for vitamin B12 deficiency: comparison between the sublingual and oral route. Br J Clin Pharmacol. 2003 Dec;56(6):635-8.
https://www.ncbi.nlm.nih.gov/pmc/articles/PMC1884303
http://www.ncbi.nlm.nih.gov/pubmed/14616423?tool=bestpractice.com
[88]Slot WB, Merkus FW, Van Deventer SJ, et al. Normalization of plasma vitamin B12 concentration by intranasal hydroxocobalamin in vitamin B12-deficient patients. Gastroenterology. 1997 Aug;113(2):430-3.
http://www.ncbi.nlm.nih.gov/pubmed/9247460?tool=bestpractice.com
[89]Parry-Strong A, Langdana F, Haeusler S, et al. Sublingual vitamin B12 compared to intramuscular injection in patients with type 2 diabetes treated with metformin: a randomised trial. N Z Med J. 2016 Jun 10;129(1436):67-75.
http://www.ncbi.nlm.nih.gov/pubmed/27355231?tool=bestpractice.com
Intranasal cyanocobalamin may be considered in patients who have undergone bariatric surgery.[74]Mechanick JI, Apovian C, Brethauer S, et al; American Association of Clinical Endocrinologists; Obesity Society; American Society for Metabolic & Bariatric Surgery. Clinical practice guidelines for the perioperative nutritional, metabolic, and nonsurgical support of the bariatric surgery patient - 2019 update. Endocr Pract. 2019 Dec;25(12):1346-59.
https://www.aace.com/disease-state-resources/nutrition-and-obesity/clinical-practice-guidelines/clinical-practice-1
http://www.ncbi.nlm.nih.gov/pubmed/31682518?tool=bestpractice.com
Patients presenting with severe symptoms
Patients presenting with severe haematological (pancytopenia and marked symptomatic anaemia) or neurological (sub-acute combined spinal degeneration, dementia, or cognitive impairment) symptoms of vitamin B12 deficiency require acute and urgent treatment.[90]Carmel R. How I treat cobalamin (vitamin B12) deficiency. Blood. 2008 Sep 15;112(6):2214-21.
https://www.ncbi.nlm.nih.gov/pmc/articles/PMC2532799
http://www.ncbi.nlm.nih.gov/pubmed/18606874?tool=bestpractice.com
Patients with symptomatic anaemia and pancytopenia require hospital admission and haematological consultant referral, and, rarely, may require red blood cell (RBC) transfusion. If there are signs of congestive cardiac failure, packed RBCs should be given together with low-dose diuretic therapy. An acute regimen of parenteral cyanocobalamin is given until significant reticulocytosis is seen in the marrow.[91]Butler CC, Vidal-Alaball J, Cannings-John R, et al. Oral vitamin B12 versus intramuscular vitamin B12 for vitamin B12 deficiency: a systematic review of randomized controlled trials. Fam Pract. 2006 Jun;23(3):279-85.
https://academic.oup.com/fampra/article/23/3/279/476697
http://www.ncbi.nlm.nih.gov/pubmed/16585128?tool=bestpractice.com
Folic acid supplementation may help reverse the haematological abnormalities.
Replacement therapy may potentially improve cognition outcomes in patients with noted cognitive impairment and vitamin B12 deficiency.[92]Jatoi S, Hafeez A, Riaz SU, et al. Low vitamin B12 levels: an underestimated cause of minimal cognitive impairment and dementia. Cureus. 2020 Feb 13;12(2):e6976.
https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7077099
http://www.ncbi.nlm.nih.gov/pubmed/32206454?tool=bestpractice.com
Patients with severe neurological symptoms may require neurological and psychogeriatric referral and evaluation while commencing the acute parenteral treatment regimen. In some cases, neurological symptoms may be irreversible despite normalisation of serum vitamin B12 levels.
Ongoing maintenance treatment is with once-daily oral cyanocobalamin, or once-monthly parenteral cyanocobalamin.
Patients with mild to moderate symptoms
Acute and maintenance treatment of patients with mild to moderate symptoms of vitamin B12 deficiency (e.g., mild anaemia, dysaesthesia/paraesthesias, polyneuropathy, depression) is with once-daily oral cyanocobalamin or once-monthly parenteral cyanocobalamin, depending on clinician preference. Patients treated with oral cyanocobalamin should respond within 8 weeks. If serum vitamin B12 does not rise significantly after this time, clinicians should switch to parenteral cyanocobalamin (if not already used), or consider other causes.
Asymptomatic or borderline deficiency in high-risk patients
High-risk patients (e.g., older patients, and those with restrictive diets or chronic GI illness) should be monitored for vitamin B12 deficiency. Treatment with oral or parenteral cyanocobalamin should be considered, even if they are asymptomatic. This is because the haematological and neurological complications of vitamin B12 deficiency may be irreversible once they develop. In the UK, guidelines recommend considering an empirical trial of treatment with low-dose cyanocobalamin for 1 month in patients with serum cobalamin levels of borderline (subclinical) deficiency on two occasions.[1]Devalia V, Hamilton MS, Molloy AM; British Committee for Standards in Haematology. Guidelines for the diagnosis and treatment of cobalamin and folate disorders. Br J Haematol. 2014 Aug;166(4):496-513.
http://onlinelibrary.wiley.com/doi/10.1111/bjh.12959/full
http://www.ncbi.nlm.nih.gov/pubmed/24942828?tool=bestpractice.com
Older patients (>65 years)
Dietary advice should be given on the importance of eating animal-derived foods (such as meat, fish, eggs, and milk), and taking multivitamin supplements. Older people who have a poor diet should be counselled that lifelong monitoring and supplements may be required.
Vegan or strict vegetarian diet
Should be counselled to supplement their diet with appropriate vitamin B12-fortified foods and multivitamin supplements in order to meet the recommended dietary allowance of 2.4 micrograms/day.[58]National Institutes of Health, Office of Dietary Supplements. Dietary supplement fact sheet: vitamin B12. 2022 [internet publication].
https://ods.od.nih.gov/factsheets/VitaminB12-HealthProfessional
[93]Del Bo' C, Riso P, Gardana C, et al. Effect of two different sublingual dosages of vitamin B12 on cobalamin nutritional status in vegans and vegetarians with a marginal deficiency: A randomized controlled trial. Clin Nutr. 2019 Apr;38(2):575-583.
https://www.clinicalnutritionjournal.com/article/S0261-5614(18)30071-2/fulltext
http://www.ncbi.nlm.nih.gov/pubmed/29499976?tool=bestpractice.com
Chronic GI illness
Patients with chronic GI illness that can cause malabsorption or inadequate absorption (e.g., pernicious anaemia, Crohn's disease, coeliac disease) or who have undergone gastric surgery or terminal ileectomy should be treated with parenteral cyanocobalamin.[1]Devalia V, Hamilton MS, Molloy AM; British Committee for Standards in Haematology. Guidelines for the diagnosis and treatment of cobalamin and folate disorders. Br J Haematol. 2014 Aug;166(4):496-513.
http://onlinelibrary.wiley.com/doi/10.1111/bjh.12959/full
http://www.ncbi.nlm.nih.gov/pubmed/24942828?tool=bestpractice.com
[94]Bischoff SC, Escher J, Hébuterne X, et al. ESPEN practical guideline: clinical nutrition in inflammatory bowel disease. Clin Nutr. 2020 Mar;39(3):632-53.
https://www.doi.org/10.1016/j.clnu.2019.11.002
http://www.ncbi.nlm.nih.gov/pubmed/32029281?tool=bestpractice.com
Bariatric surgery
Patients who have had bariatric surgery may not be able to adequately maintain serum vitamin B12 levels with multivitamins; therefore, oral, parenteral, or intranasal cyanocobalamin should be given.[74]Mechanick JI, Apovian C, Brethauer S, et al; American Association of Clinical Endocrinologists; Obesity Society; American Society for Metabolic & Bariatric Surgery. Clinical practice guidelines for the perioperative nutritional, metabolic, and nonsurgical support of the bariatric surgery patient - 2019 update. Endocr Pract. 2019 Dec;25(12):1346-59.
https://www.aace.com/disease-state-resources/nutrition-and-obesity/clinical-practice-guidelines/clinical-practice-1
http://www.ncbi.nlm.nih.gov/pubmed/31682518?tool=bestpractice.com
[95]Mahawar KK, Reid A, Graham Y, et al. Oral vitamin B12 supplementation after Roux-en-Y gastric bypass: a systematic review. Obes Surg. 2018 Jul;28(7):1916-23.
http://www.ncbi.nlm.nih.gov/pubmed/29318504?tool=bestpractice.com
An oral multivitamin supplement optimised for bariatric surgery has shown potential benefit in reducing vitamin deficiencies following Roux-en-Y gastric bypass surgery, but the evidence is limited.[96]Homan J, Schijns W, Aarts EO, et al. An optimized multivitamin supplement lowers the number of vitamin and mineral deficiencies three years after Roux-en-Y gastric bypass: a cohort study. Surg Obes Relat Dis. 2016 Mar-Apr;12(3):659-67.
http://www.ncbi.nlm.nih.gov/pubmed/26947791?tool=bestpractice.com
Pregnancy and breastfeeding
Up to 20% to 30% of pregnant women may be at risk for vitamin B12 deficiency.[11]Sukumar N, Saravanan P. Investigating vitamin B12 deficiency. BMJ. 2019 May 10;365:l1865.
http://www.ncbi.nlm.nih.gov/pubmed/31076395?tool=bestpractice.com
Deficiency found in pregnancy should be treated, even if the woman is asymptomatic, because deficiency may be associated with adverse risk for preterm delivery and lower birth weight.[11]Sukumar N, Saravanan P. Investigating vitamin B12 deficiency. BMJ. 2019 May 10;365:l1865.
http://www.ncbi.nlm.nih.gov/pubmed/31076395?tool=bestpractice.com
[29]Rashid S, Meier V, Patrick H. Review of vitamin B12 deficiency in pregnancy: a diagnosis not to miss as veganism and vegetarianism become more prevalent. Eur J Haematol. 2021 Apr;106(4):450-5.
https://onlinelibrary.wiley.com/doi/10.1111/ejh.13571
http://www.ncbi.nlm.nih.gov/pubmed/33341967?tool=bestpractice.com
[57]Rogne T, Tielemans MJ, Chong MF, et al. Associations of maternal vitamin B12 concentration in pregnancy with the risks of preterm birth and low birth weight: a systematic review and meta-analysis of individual participant data. Am J Epidemiol. 2017 Feb 1;185(3):212-23.
https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5390862
http://www.ncbi.nlm.nih.gov/pubmed/28108470?tool=bestpractice.com
Treatment of pregnant women is generally the same as for non-pregnant patients.
Pregnant and breastfeeding women who have a strict vegetarian or vegan diet should be counselled about adequate intake of vitamin B12 and supplementation.[29]Rashid S, Meier V, Patrick H. Review of vitamin B12 deficiency in pregnancy: a diagnosis not to miss as veganism and vegetarianism become more prevalent. Eur J Haematol. 2021 Apr;106(4):450-5.
https://onlinelibrary.wiley.com/doi/10.1111/ejh.13571
http://www.ncbi.nlm.nih.gov/pubmed/33341967?tool=bestpractice.com
Breastfeeding women who adhere to a vegan diet will only provide adequate vitamin B12 for their infant if the mother satisfies vitamin B12 requirements through supplementation.[97]Procter SB, Campbell CG. Position of the Academy of Nutrition and Dietetics: nutrition and lifestyle for a healthy pregnancy outcome. J Acad Nutr Diet. 2014 Jul;114(7):1099-103.
https://www.doi.org/10.1016/j.jand.2014.05.005
http://www.ncbi.nlm.nih.gov/pubmed/24956993?tool=bestpractice.com
Monitoring response to treatment
Brisk reticulocytosis in the bone marrow occurs within 1-2 weeks of initiating treatment in patients with severe anaemia due to vitamin B12 deficiency.
Other markers of deficiency, including methylmalonic acid, homocysteine, and mean corpuscular volume, should normalise in 8 weeks with adequate treatment. Serum vitamin B12 (serum cobalamin) levels should return to normal before starting maintenance therapy.
Maintenance therapy
Most patients identified with vitamin B12 deficiency require lifelong maintenance therapy with once-daily oral cyanocobalamin, or once-monthly parenteral cyanocobalamin. Oral cyanocobalamin is generally well tolerated for maintenance. Parenteral cyanocobalamin is often reserved for those who cannot take daily pills or have documented failure to oral therapy. It may also be considered when there are concerns about adherence to oral vitamin B12 replacement therapy.[98]Iacobucci G. Consider intramuscular injections for older people with vitamin B(12) deficiency, says NICE. BMJ. 2023 Jul 11;382:1604.
http://www.ncbi.nlm.nih.gov/pubmed/37433611?tool=bestpractice.com
Some clinicians may attempt to lower the effective dose of maintenance oral cyanocobalamin. Periodic monitoring after replacement may be able to identify patients who may maintain serum levels with oral doses <1000 micrograms/day.[99]Andrès E, Dali-Youcef N, Vogel T, et al. Oral cobalamin (vitamin B(12)) treatment: an update. Int J Lab Hematol. 2009 Feb;31(1):1-8.
https://onlinelibrary.wiley.com/doi/10.1111/j.1751-553X.2008.01115.x
http://www.ncbi.nlm.nih.gov/pubmed/19032377?tool=bestpractice.com
However, absorption may be variable, and some patients may experience less than maximal clinical and laboratory response with oral cyanocobalamin doses <1000 micrograms/day.[100]Rajan S, Wallace JI, Brodkin KI, et al. Response of elevated methylmalonic acid to three dose levels of oral cobalamin in older adults. J Am Geriatr Soc. 2002 Nov;50(11):1789-95.
http://www.ncbi.nlm.nih.gov/pubmed/12410896?tool=bestpractice.com
[101]Eussen SJ, de Groot LC, Clarke R, et al. Oral cyanocobalamin supplementation in older people with vitamin B12 deficiency: a dose-finding trial. Arch Intern Med. 2005 May 23;165(10):1167-72.
http://archinte.ama-assn.org/cgi/content/full/165/10/1167
http://www.ncbi.nlm.nih.gov/pubmed/15911731?tool=bestpractice.com
[102]Andrès E, Fothergill H, Mecili M. Efficacy of oral cobalamin (vitamin B12) therapy. Expert Opin Pharmacother. 2010 Feb;11(2):249-56.
http://www.ncbi.nlm.nih.gov/pubmed/20088746?tool=bestpractice.com